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Therapeutic landscape for inherited ocular diseases: current and emerging therapies
Inherited ocular diseases comprise a heterogeneous group of rare and complex diseases, including inherited retinal diseases (IRDs) and inherited optic neuropathies. Recent success in adeno-associated virus-based gene therapy, voretigene neparvovec (Luxturna(®)) for RPE65-related IRDs, has heralded r...
Autores principales: | Chan, Hwei Wuen, Oh, Jaslyn, Leroy, Bart |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Wolters Kluwer - Medknow
2023
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9979805/ https://www.ncbi.nlm.nih.gov/pubmed/36722513 http://dx.doi.org/10.4103/singaporemedj.SMJ-2022-179 |
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