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The future of sickle cell disease therapeutics rests in genomics

Sickle cell disease (SCD) is the most-common monogenic recessive disease in humans, annually affecting almost 300,000 newborns worldwide, 75% of whom live in Africa. Genomics research can accelerate the development of curative therapies for SCD in three ways. First, research should explore the missi...

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Detalles Bibliográficos
Autor principal:	Wonkam, Ambroise
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	The Company of Biologists Ltd 2023
Materias:	Perspective
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9983775/ https://www.ncbi.nlm.nih.gov/pubmed/36815490 http://dx.doi.org/10.1242/dmm.049765

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