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Mutation-independent gene knock-in therapy targeting 5′UTR for autosomal dominant retinitis pigmentosa

Detalles Bibliográficos
Autores principales:	Hoang, Duc Anh, Liao, Baoshan, Zheng, Zongli, Xiong, Wenjun
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Nature Publishing Group UK 2023
Materias:	Letter
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC9992370/ https://www.ncbi.nlm.nih.gov/pubmed/36882423 http://dx.doi.org/10.1038/s41392-022-01308-0

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