5559749 A MULTICENTER, RETROSPECTIVE STUDY ON REAL-WORLD EXPERIENCE OF PATIENTS WITH SICKLE CELL DISEASE TREATED WITH VOXELOTOR

por Andemariam, B., Idowu, M., Shah, N., Drachtman, R., Sharma, A., Glaros, A., Achebe, M., Nero, A., Curtis, S., Minniti, C.
Publicado 2023

5613022 SOCIETAL BURDEN OF SICKLE CELL DISEASE IN THE UK: EMPIRICAL ESTIMATES OF PRODUCTIVITY LOSS AND LOSS OF FUTURE INCOME USING REAL-WORLD EVIDENCE

por Besser, M., Jarvis, S., Hamlyn, M., Brown, J.P., Barcelos, G., Beaubrun, A., Binns, M., Rice, C.T.
Publicado 2023

5589320 FOLLOW-UP RESULTS OF A PHASE 2 STUDY ASSESSING THE SAFETY AND EFFICACY OF MITAPIVAT TREATMENT, AN ORAL PYRUVATE KINASE ACTIVATOR, FOR UP TO 60 WEEKS IN SUBJECTS WITH SICKLE...

por van Dijk, M.J., Rab, M.A.E., van Oirschot, B.A., Bos, J.F., Derichs, C., Rijneveld, A.W., Cnossen, M.H., Nur, E., Biemond, B.J., Bartels, M., Jans, J.J.M., van Solinge, W.W., Schutgens, R.E.G., van Wijk, R., van Beers, E.J.
Publicado 2023

5612617 EFFICACY AND SAFETY OF A SINGLE DOSE OF EXAGAMGLOGENE AUTOTEMCEL FOR TRANSFUSION-DEPENDENT-THALASSEMIA AND SEVERE SICKLE CELL DISEASE

por de la Fuente, J., Locatelli, F., Frangoul, H., Corbacioglu, S., Wall, D., Cappellini, M., de Montalembert, M., Kattamis, A., Lobitz, S., Rondelli, D., Sheth, S., Steinberg, M., Walters, M., Bobruff, Y., Simard, C., Song, Y., Zhang, L., Sharma, A., Imren, S., Hobbs, B., Grupp, S.
Publicado 2023

5595849 THE GUT MICROBIOME AND HYDROXYUREA EFFECT ON SICKLE CELL DISEASE CHILDREN FROM ANGOLA

por Brito, M., Delgadinho, M., Ginete, C., Santos, B., Vasconcelos, J.
Publicado 2023

5613275 USE OF CONSUMER WEARABLES TO PREDICT PAIN IN PATIENTS WITH SICKLE CELL DISEASE

por Vuong, C., Mallikarjunan, A., Utkarsh, K., Stojancic, R., Shah, N.
Publicado 2023

5613049 THE DIAGNOSTIC ACCURACY AND REPEATABILITY OF AN ARTIFICIAL INTELLIGENCE BASED SYSTEM TO OBTAIN AUTOMATED LIVER IRON CONCENTRATION MEASUREMENTS USING MAGNETIC RESONANCE IMAG...

por St Pierre, T.G., Aydinok, Y., El-Beshlawy, A., Bayraktaroglu, S., Ibrahim, A., Hamdy, M., Pang, W., Khorshid, S., Bangma, S., House, M.
Publicado 2023

5613511 URINARY KIDNEY INJURY MOLECULE 1 AND URINARY MONOCYTE CHEMOTACTIC PROTEIN 1 AS NOVEL BIOMARKERS FOR EARLY DIAGNOSIS OF SICKLE CELL RENAL DYSFUNCTION

por Hussien, N.I.H., Elalfy, M.S.E., Adly, A.A.A., Mansour, M.A.M.
Publicado 2023

5610603 CLINICAL AND GENETIC PREDICTORS OF SICKLE CELL NEPHROPATHY IN MALAWI

por Banda, K.H.B., Morrice, J.M., Chagaluka, G.C., Nembaware, V.N., Wonkam, A.W.
Publicado 2023

5613514 PAVING THE WAY FOR GENETIC MEDICINE IN SUB-SAHARAN AFRICA: A REPORT ON THE FIRST GENETIC COUNSELLING PROGRAM IN THE REGION

por Osae-Larbi, J.A., Ofori-Acquah, S.F., Anie, K.A., Osei-Tutu, A.
Publicado 2023

5596911 RETINAL AND MACULAR AFFECTION IN EGYPTIAN SICKLE CELL DISEASE PATIENTS USING SPECTRAL DOMAIN OCT AND OCT-ANGIOGRAPHY: A SINGLE CENTER STUDY

por El-Ghamrawy, M., Zedan, R.H., Omar, A.R., Salama, N.
Publicado 2023

5610726 EXPERIENCE OF LIFE FOR CHILDREN AND YOUNG PEOPLE WITH SICKLE CELL DISORDERS: LESSONS LEARNED FROM A PUBLIC ENGAGEMENT EVENT

por Pillay, K., Satar, A., Roberts, R., Wilkey, O., Younis, J., Leigh, A.
Publicado 2023

5613393 PREGNANCY OUTCOMES IN WOMEN WITH SICKLE CELL DISEASE IN IRELAND: A RETROSPECTIVE REVIEW

por Ryan, E., Allen, A., Ngwenya, N., Sheehan, C., Manning, C., Byrne, B., Lynch, C., Regan, C., Tuohy, E.
Publicado 2023

5610437 HLA TISSUE TYPING AND HSCT FOR THE SICKLE CELL DISEASE COHORT AT THE ROYAL CHILDREN’S HOSPITAL (MELBOURNE, AUSTRALIA): AN AUDIT

por Duncan, A., Clucas, L., O’Reilly, E., Greenway, A.
Publicado 2023

5558131 GENETICS OF IRANIAN ALPHA THALASSEMIA PATIENTS; COMPREHENSIVE ORIGINAL STUDY

por Khosravi, A., Karimzadeh, M., Takhviji, V.
Publicado 2023

5607560 AN AUDIT OF COMPLIANCE WITH NEONATAL SCREENING GUIDELINES IN NEONATES DIAGNOSED WITH SICKLE CELL DISEASE IN SOUTH WALES

por Pasha, S.R.P., Playford, S.P., Thakur, I.T.
Publicado 2023

5567917 COST COMPARISON OF TRANSFUSION CHOICES IN OMAN FOR PATIENTS SUFFERING FROM SICKLE CELL DISEASE

por Sweerts, L., Al Kindi, S., Al Hashami, S., Doshi, S., Dierick, K.
Publicado 2023

5613341 REAL-WORLD CHANGES IN KIDNEY FUNCTION FOR PATIENTS WITH SICKLE CELL DISEASE OR OTHER ANAEMIAS RECEIVING IRON CHELATION THERAPY IN THE US

por Sunil Bhandari, S.B., Emmeline Igboekwe, E.I., Noemi Toiber Temin, N.T.T., Khashayar Azimpour, K.A., Jonathan Alsop, J.A., Caroline Fradette, C.F., Fernando Tricta, F.T.
Publicado 2023

5609968 REAL-WORLD PATIENT-REPORTED OUTCOMES AND WEARABLE METRIC CORRELATIONS: REMOTE DAILY MONITORING FOR EXPLORATION OF QUALITY OF LIFE IN SICKLE CELL DISEASE

por Agrippa, O.A., Summers, K.Z., Anie, K.A., Telfer, P., Lugthart, S.
Publicado 2023

5613417 CO-TREATMENT OF ERYTHROID CELLS ISOLATED FROM Β039-THALASSEMIA PATIENTS WITH CRISPR-CAS9 GENE EDITING AND FETAL HEMOGLOBIN INDUCTION

por Lipucci di Paola, M.L.P., Lucia Carmela Cosenza, L.C.C., Cristina Zuccato, C.Z., Matteo Zurlo, M.Z., Roberto Gambari, R.G., Alessia Finotti, A.F.
Publicado 2023