A Brief Review of Duchenne Muscular Dystrophy Treatment Options, with an Emphasis on Two Novel Strategies

Despite the full cloning of the Dystrophin cDNA 35 years ago, no effective treatment exists for the Duchenne Muscular Dystrophy (DMD) patients who have a mutation in this gene. Many treatment options have been considered, investigated preclinically and some clinically, but none have circumvented all...

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Detalles Bibliográficos
Autores principales: Heydemann, Ahlke, Siemionow, Maria
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2023
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10044847/
https://www.ncbi.nlm.nih.gov/pubmed/36979809
http://dx.doi.org/10.3390/biomedicines11030830

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10044847/
https://www.ncbi.nlm.nih.gov/pubmed/36979809
http://dx.doi.org/10.3390/biomedicines11030830

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