Cargando…
A Brief Review of Duchenne Muscular Dystrophy Treatment Options, with an Emphasis on Two Novel Strategies
Despite the full cloning of the Dystrophin cDNA 35 years ago, no effective treatment exists for the Duchenne Muscular Dystrophy (DMD) patients who have a mutation in this gene. Many treatment options have been considered, investigated preclinically and some clinically, but none have circumvented all...
Autores principales: | Heydemann, Ahlke, Siemionow, Maria |
---|---|
Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2023
|
Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10044847/ https://www.ncbi.nlm.nih.gov/pubmed/36979809 http://dx.doi.org/10.3390/biomedicines11030830 |
Ejemplares similares
-
Skeletal Muscle Metabolism in Duchenne and Becker Muscular Dystrophy—Implications for Therapies
por: Heydemann, Ahlke
Publicado: (2018) -
Dystrophin Expressing Chimeric (DEC) Human Cells Provide a Potential Therapy for Duchenne Muscular Dystrophy
por: Siemionow, Maria, et al.
Publicado: (2018) -
Intraosseous transplant of dystrophin expressing chimeric (DEC) cells improves skeletal muscle function in mdx mouse model of Duchenne muscular dystrophy
por: Malik, Mohammad, et al.
Publicado: (2021) -
Human dystrophin expressing chimeric (DEC) cell therapy ameliorates cardiac, respiratory, and skeletal muscle's function in Duchenne muscular dystrophy
por: Siemionow, Maria, et al.
Publicado: (2021) -
Long-Term Biodistribution and Safety of Human Dystrophin Expressing Chimeric Cell Therapy After Systemic-Intraosseous Administration to Duchenne Muscular Dystrophy Model
por: Siemionow, Maria, et al.
Publicado: (2022)