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Gene Therapy for β-Hemoglobinopathies: From Discovery to Clinical Trials

Investigations to understand the function and control of the globin genes have led to some of the most exciting molecular discoveries and biomedical breakthroughs of the 20th and 21st centuries. Extensive characterization of the globin gene locus, accompanied by pioneering work on the utilization of...

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Detalles Bibliográficos
Autores principales: Segura, Eva Eugenie Rose, Ayoub, Paul George, Hart, Kevyn Lopez, Kohn, Donald Barry
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2023
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10054523/
https://www.ncbi.nlm.nih.gov/pubmed/36992422
http://dx.doi.org/10.3390/v15030713