Cargando…
Gene Therapy for β-Hemoglobinopathies: From Discovery to Clinical Trials
Investigations to understand the function and control of the globin genes have led to some of the most exciting molecular discoveries and biomedical breakthroughs of the 20th and 21st centuries. Extensive characterization of the globin gene locus, accompanied by pioneering work on the utilization of...
Autores principales: | Segura, Eva Eugenie Rose, Ayoub, Paul George, Hart, Kevyn Lopez, Kohn, Donald Barry |
---|---|
Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2023
|
Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10054523/ https://www.ncbi.nlm.nih.gov/pubmed/36992422 http://dx.doi.org/10.3390/v15030713 |
Ejemplares similares
-
Unexpected discovery of hemoglobinopathy C/β° thalassemia
por: Bouyarmane, Wafaa, et al.
Publicado: (2018) -
Gene Therapy for Hemoglobinopathies
por: Cavazzana, Marina, et al.
Publicado: (2018) -
Gene Therapy of the Hemoglobinopathies
por: Kunz, Joachim B., et al.
Publicado: (2020) -
Gene Therapy in Thalassemia and Hemoglobinopathies
por: Breda, Laura, et al.
Publicado: (2009) -
Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the β(A(T87Q))-Globin Gene
por: Negre, Olivier, et al.
Publicado: (2016)