Identifying responders to elamipretide in Barth syndrome: Hierarchical clustering for time series data

BACKGROUND: Barth syndrome (BTHS) is a rare genetic disease that is characterized by cardiomyopathy, skeletal myopathy, neutropenia, and growth abnormalities and often leads to death in childhood. Recently, elamipretide has been tested as a potential first disease-modifying drug. This study aimed to...

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Detalles Bibliográficos
Autores principales: Van den Eynde, Jef, Chinni, Bhargava, Vernon, Hilary, Thompson, W. Reid, Hornby, Brittany, Kutty, Shelby, Manlhiot, Cedric
Formato: Online Artículo Texto
Lenguaje:English
Publicado: BioMed Central 2023
Materias:
Research
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10088720/
https://www.ncbi.nlm.nih.gov/pubmed/37041653
http://dx.doi.org/10.1186/s13023-023-02676-8

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10088720/
https://www.ncbi.nlm.nih.gov/pubmed/37041653
http://dx.doi.org/10.1186/s13023-023-02676-8

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