A Review of CRISPR Tools for Treating Usher Syndrome: Applicability, Safety, Efficiency, and In Vivo Delivery

This review considers research into the treatment of Usher syndrome, a deaf-blindness syndrome inherited in an autosomal recessive manner. Usher syndrome mutations are markedly heterogeneous, involving many different genes, and research grants are limited due to minimal patient populations. Furtherm...

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Detalles Bibliográficos
Autores principales: Major, Lauren, McClements, Michelle E., MacLaren, Robert E.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2023
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10146473/
https://www.ncbi.nlm.nih.gov/pubmed/37108761
http://dx.doi.org/10.3390/ijms24087603

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10146473/
https://www.ncbi.nlm.nih.gov/pubmed/37108761
http://dx.doi.org/10.3390/ijms24087603

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