A retrospective survey of patients with hereditary transthyretin-mediated (hATTR) amyloidosis treated with patisiran in real-world clinical practice in Belgium

INTRODUCTION: Hereditary transthyretin-mediated (hATTR) amyloidosis, a genetic disease caused by mutations in the transthyretin gene, leads to progressive sensory and autonomic neuropathy and/or cardiomyopathy and is associated with renal and ophthalmologic manifestations and a poor prognosis. METHO...

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Detalles Bibliográficos
Autores principales: De Bleecker, Jan L., Claeys, Kristl G., Delstanche, Stéphanie, Van Parys, Vinciane, Baets, Jonathan, Tilleux, Sébastien, Remiche, Gauthier
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer International Publishing 2023
Materias:
Original Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10238330/
https://www.ncbi.nlm.nih.gov/pubmed/36829087
http://dx.doi.org/10.1007/s13760-023-02188-z

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10238330/
https://www.ncbi.nlm.nih.gov/pubmed/36829087
http://dx.doi.org/10.1007/s13760-023-02188-z

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