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In Vitro FVIII-Encoding Transgenic Mesenchymal Stem Cells Maintain Successful Coagulation in FVIII-Deficient Plasma Mimicking Hemophilia A

OBJECTIVE: Hemophilia A is an X-linked recessive bleeding disorder caused by a deficiency of plasma coagulation factor VIII (FVIII), and it accounts for about 80%-85% of all cases of hemophilia. Plasma-derived therapies or recombinant FVIII concentrates are used to prevent and treat the bleeding sym...

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Detalles Bibliográficos
Autores principales: Hemşinlioğlu, Cansu, Aslan, Elif Sibel, Taştan, Cihan, Çakırsoy, Didem, Turan, Raife Dilek, Seyis, Utku, Elek, Muhammer, Karakuş, Gözde Sır, Günaydın, Ömür Selin, Abanuz, Selen, Kançağı, Derya Dilek, Yurtsever, Bulut, Yalçın, Koray, Kasap, Murat, Ovalı, Ercüment
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Galenos Publishing 2023
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10240160/
https://www.ncbi.nlm.nih.gov/pubmed/37022209
http://dx.doi.org/10.4274/tjh.galenos.2023.2022-0318