Rapid and Reliable Quantification of Prime Editing Targeting Within the Porcine ABCA4 Gene Using a BRET-Based Sensor

Stargardt disease (STGD) leads to blindness in children and young adults. So far, no curative therapy is available and gene augmentation therapies have not yet advanced to the clinics, in part, due to the limited packaging capacity of adeno-associated viruses used to transfer genes into photorecepto...

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Detalles Bibliográficos
Autores principales: Wimmer, Tobias, Sawinski, Hannah, Urban, Anne M., Motlik, Jan, Stieger, Knut
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Mary Ann Liebert, Inc., publishers 2023
Materias:
Original Papers
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10278032/
https://www.ncbi.nlm.nih.gov/pubmed/36857739
http://dx.doi.org/10.1089/nat.2022.0037

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10278032/
https://www.ncbi.nlm.nih.gov/pubmed/36857739
http://dx.doi.org/10.1089/nat.2022.0037

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