Acceso a medicamentos huérfanos para el tratamiento de la atrofia muscular espinal en España

INTRODUCTION. Spinal muscular atrophy (SMA) is a rare disease whose diagnosis and treatment are complex. In Spain, there are two orphan medicines that are currently financed by the state, nusinersen and onasemnogene abeparvovec and, a third in process, risdiplam. The objective was to detect possible...

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Detalles Bibliográficos
Autores principales: García-Parra, Beliu, Guiu, Josep M., Modamio, Pilar, Martínez-Yélamos, Antonio, Mariño-Hernández, Eduardo L., Povedano, Mónica
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Viguera Editores (Evidenze Group) 2022
Materias:
Original
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10280711/
https://www.ncbi.nlm.nih.gov/pubmed/36285446
http://dx.doi.org/10.33588/rn.7509.2022298

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10280711/
https://www.ncbi.nlm.nih.gov/pubmed/36285446
http://dx.doi.org/10.33588/rn.7509.2022298

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