Gene therapy has recently become a realistic treatment perspective for patients with hemophilia. Reviewing the literature and our personal experience from clinical trials, we discuss key aspects of hemophilia A and B gene therapy with vectors derived from adeno-associated virus, including predictabl...

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Detalles Bibliográficos
Autores principales: Miesbach, Wolfgang, Oldenburg, Johannes, Klamroth, Robert, Eichler, Hermann, Koscielny, Jürgen, Holzhauer, Susanne, Holstein, Katharina, Hovinga, Johanna A. Kremer, Alberio, Lorenzo, Olivieri, Martin, Knöfler, Ralf, Male, Christoph, Tiede, Andreas
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Georg Thieme Verlag KG 2022
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10281774/
https://www.ncbi.nlm.nih.gov/pubmed/36516966
http://dx.doi.org/10.1055/a-1957-4477

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10281774/
https://www.ncbi.nlm.nih.gov/pubmed/36516966
http://dx.doi.org/10.1055/a-1957-4477

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