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Gene therapy has recently become a realistic treatment perspective for patients with hemophilia. Reviewing the literature and our personal experience from clinical trials, we discuss key aspects of hemophilia A and B gene therapy with vectors derived from adeno-associated virus, including predictabl...

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Detalles Bibliográficos
Autores principales:	Miesbach, Wolfgang, Oldenburg, Johannes, Klamroth, Robert, Eichler, Hermann, Koscielny, Jürgen, Holzhauer, Susanne, Holstein, Katharina, Hovinga, Johanna A. Kremer, Alberio, Lorenzo, Olivieri, Martin, Knöfler, Ralf, Male, Christoph, Tiede, Andreas
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Georg Thieme Verlag KG 2022
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10281774/ https://www.ncbi.nlm.nih.gov/pubmed/36516966 http://dx.doi.org/10.1055/a-1957-4477

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