Gene Therapy Approaches for the Treatment of Hemophilia B

In contrast to the standard enzyme-replacement therapy, administered from once per 7–14 days to 2–3 times a week in patients with severe hemophilia B, as a result of a single injection, gene therapy can restore F9 gene expression and maintain it for a prolonged time. In clinical research, the approa...

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Detalles Bibliográficos
Autores principales: Soroka, Anastasiia B., Feoktistova, Sofya G., Mityaeva, Olga N., Volchkov, Pavel Y.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2023
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10341900/
https://www.ncbi.nlm.nih.gov/pubmed/37445943
http://dx.doi.org/10.3390/ijms241310766

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10341900/
https://www.ncbi.nlm.nih.gov/pubmed/37445943
http://dx.doi.org/10.3390/ijms241310766

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