Dystrophin Expressing Chimeric (DEC) Cell Therapy for Duchenne Muscular Dystrophy: A First-in-Human Study with Minimum 6 Months Follow-up

Duchenne Muscular Dystrophy (DMD) is a X-linked progressive lethal muscle wasting disease for which there is no cure. We present first-in-human study assessing safety and efficacy of novel Dystrophin Expressing Chimeric (DEC) cell therapy created by fusion of patient myoblasts with myoblasts of norm...

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Detalles Bibliográficos
Autores principales: Heydemann, Ahlke, Bieganski, Grzegorz, Wachowiak, Jacek, Czarnota, Jarosław, Niezgoda, Adam, Siemionow, Krzysztof, Ziemiecka, Anna, Sikorska, Maria H., Bozyk, Katarzyna, Tullius, Stefan G., Siemionow, Maria
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer US 2023
Materias:
Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10366026/
https://www.ncbi.nlm.nih.gov/pubmed/37000376
http://dx.doi.org/10.1007/s12015-023-10530-4

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10366026/
https://www.ncbi.nlm.nih.gov/pubmed/37000376
http://dx.doi.org/10.1007/s12015-023-10530-4

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