Assessment of Therapeutic Potential of a Dual AAV Approach for Duchenne Muscular Dystrophy

Duchenne muscular dystrophy (DMD) is a yet incurable rare genetic disease that affects the skeletal and cardiac muscles, leading to progressive muscle wasting and premature death. DMD is caused by the lack of dystrophin, a muscle protein essential for the biochemical support and integrity of muscle...

Descripción completa

Detalles Bibliográficos
Autores principales: Albini, Sonia, Palmieri, Laura, Dubois, Auriane, Bourg, Nathalie, Lostal, William, Richard, Isabelle
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2023
Materias:
Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10380683/
https://www.ncbi.nlm.nih.gov/pubmed/37511179
http://dx.doi.org/10.3390/ijms241411421

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10380683/
https://www.ncbi.nlm.nih.gov/pubmed/37511179
http://dx.doi.org/10.3390/ijms241411421

Ejemplares similares