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Vamorolone improves Becker muscular dystrophy and increases dystrophin protein in bmx model mice
There is no approved therapy for Becker muscular dystrophy (BMD), a genetic muscle disease caused by in-frame dystrophin deletions. We previously developed the dissociative corticosteroid vamorolone for treatment of the allelic, dystrophin-null disease Duchenne muscular dystrophy. We hypothesize vam...
Autores principales: | , , , , , |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Elsevier
2023
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10391915/ https://www.ncbi.nlm.nih.gov/pubmed/37534133 http://dx.doi.org/10.1016/j.isci.2023.107161 |