Complete correction of murine phenylketonuria by selection-enhanced hepatocyte transplantation

Hepatocyte transplantation for genetic liver diseases has several potential advantages over gene therapy. However, low efficiency of cell engraftment has limited its clinical implementation. This problem could be overcome by selectively expanding transplanted donor cells until they replace enough of...

Descripción completa

Detalles Bibliográficos
Autores principales: Vonada, Anne, Wakefield, Leslie, Martinez, Michael, Harding, Cary O., Grompe, Markus, Tiyaboonchai, Amita
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Cold Spring Harbor Laboratory 2023
Materias:
Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10491101/
https://www.ncbi.nlm.nih.gov/pubmed/37693457
http://dx.doi.org/10.1101/2023.08.27.554228

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10491101/
https://www.ncbi.nlm.nih.gov/pubmed/37693457
http://dx.doi.org/10.1101/2023.08.27.554228

Ejemplares similares