Outcome Measures and Biomarkers for Clinical Trials in Hereditary Spastic Paraplegia: A Scoping Review

Hereditary spastic paraplegia (HSP) is characterized by progressive lower limb spasticity. There is no disease-modifying treatment currently available. Therefore, standardized, validated outcome measures to facilitate clinical trials are urgently needed. We performed a scoping review of outcome meas...

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Detalles Bibliográficos
Autores principales: Siow, Sue-Faye, Yeow, Dennis, Rudaks, Laura I., Jia, Fangzhi, Wali, Gautam, Sue, Carolyn M., Kumar, Kishore R.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2023
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10530989/
https://www.ncbi.nlm.nih.gov/pubmed/37761896
http://dx.doi.org/10.3390/genes14091756

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10530989/
https://www.ncbi.nlm.nih.gov/pubmed/37761896
http://dx.doi.org/10.3390/genes14091756

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