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Ocular development after highly effective modulator treatment early in life

Highly effective cystic fibrosis (CF) transmembrane conductance regulator (CFTR) modulator therapies (HEMT), including elexacaftor-tezacaftor-ivacaftor, correct the underlying molecular defect causing CF. HEMT decreases general symptom burden by improving clinical metrics and quality of life for mos...

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Detalles Bibliográficos
Autores principales: Zhu, Yimin, Li, Danni, Reyes-Ortega, Felisa, Chinnery, Holly R., Schneider-Futschik, Elena K.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Frontiers Media S.A. 2023
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10547496/
https://www.ncbi.nlm.nih.gov/pubmed/37795027
http://dx.doi.org/10.3389/fphar.2023.1265138