Exon 44 skipping in Duchenne muscular dystrophy: NS-089/NCNP-02, a dual-targeting antisense oligonucleotide

Exon-skipping therapy mediated by antisense oligonucleotides is expected to provide a therapeutic option for Duchenne muscular dystrophy. Antisense oligonucleotides for exon skipping reported so far target a single continuous sequence in or around the target exon. In the present study, we investigat...

Descripción completa

Detalles Bibliográficos
Autores principales: Watanabe, Naoki, Tone, Yuichiro, Nagata, Tetsuya, Masuda, Satoru, Saito, Takashi, Motohashi, Norio, Takagaki, Kazuchika, Aoki, Yoshitsugu, Takeda, Shin’ichi
Formato: Online Artículo Texto
Lenguaje:English
Publicado: American Society of Gene & Cell Therapy 2023
Materias:
Original Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10579524/
https://www.ncbi.nlm.nih.gov/pubmed/37854955
http://dx.doi.org/10.1016/j.omtn.2023.102034

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10579524/
https://www.ncbi.nlm.nih.gov/pubmed/37854955
http://dx.doi.org/10.1016/j.omtn.2023.102034

Ejemplares similares