A post hoc analysis of Projected Retained Ability Scores (PRAS) for the longitudinal assessment of cognitive functioning in patients with neuronopathic mucopolysaccharidosis II receiving intrathecal idursulfase-IT

BACKGROUND: Norm-based scores used to assess cognitive ability have clinical value when describing functioning of patients with neuronopathic disorders compared with unaffected, same-age peers. However, they have limitations when used to assess change in cognitive ability between two timepoints, esp...

Descripción completa

Detalles Bibliográficos
Autores principales: Yee, Karen S., Chirila, Costel, Davenport, Eric, Mladsi, Deirdre, Barnett, Christine, Kronenberger, William G.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: BioMed Central 2023
Materias:
Research
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10621086/
https://www.ncbi.nlm.nih.gov/pubmed/37915038
http://dx.doi.org/10.1186/s13023-023-02957-2

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10621086/
https://www.ncbi.nlm.nih.gov/pubmed/37915038
http://dx.doi.org/10.1186/s13023-023-02957-2

Ejemplares similares