Combination disease‐modifying treatment in spinal muscular atrophy: A proposed classification

We sought to devise a rational, systematic approach for defining/grouping survival motor neuron‐targeted disease‐modifying treatment (DMT) scenarios. The proposed classification is primarily based on a two‐part differentiation: initial DMT, and persistence/discontinuation of subsequent DMT(s). Treat...

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Detalles Bibliográficos
Autores principales: Proud, Crystal M., Mercuri, Eugenio, Finkel, Richard S., Kirschner, Janbernd, De Vivo, Darryl C., Muntoni, Francesco, Saito, Kayoko, Tizzano, Eduardo F., Desguerre, Isabelle, Quijano‐Roy, Susana, Benguerba, Kamal, Raju, Dheeraj, Faulkner, Eric, Servais, Laurent
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2023
Materias:
Brief Communications
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10646995/
https://www.ncbi.nlm.nih.gov/pubmed/37691296
http://dx.doi.org/10.1002/acn3.51889

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10646995/
https://www.ncbi.nlm.nih.gov/pubmed/37691296
http://dx.doi.org/10.1002/acn3.51889

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