Practical Guidance for the Use of Patisiran in the Management of Polyneuropathy in Hereditary Transthyretin-Mediated Amyloidosis

Variant transthyretin amyloidosis (ATTRv) is an autosomal dominant inherited genetic disorder that affects 5000–10,000 people worldwide. It is caused by mutations in the transthyretin (TTR) gene and results in amyloid deposition in a variety of organs due to abnormal accumulation of TTR protein fibr...

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Detalles Bibliográficos
Autores principales: Dixon, Stacy, Kang, Xuan, Quan, Dianna
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Dove 2023
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10691373/
https://www.ncbi.nlm.nih.gov/pubmed/38047038
http://dx.doi.org/10.2147/TCRM.S361706

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10691373/
https://www.ncbi.nlm.nih.gov/pubmed/38047038
http://dx.doi.org/10.2147/TCRM.S361706

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