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Complete Genetic Correction of iPS Cells From Duchenne Muscular Dystrophy

Human artificial chromosome (HAC) has several advantages as a gene therapy vector, including stable episomal maintenance that avoids insertional mutations and the ability to carry large gene inserts including the regulatory elements. Induced pluripotent stem (iPS) cells have great potential for gene...

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Detalles Bibliográficos
Autores principales: Kazuki, Yasuhiro, Hiratsuka, Masaharu, Takiguchi, Masato, Osaki, Mitsuhiko, Kajitani, Naoyo, Hoshiya, Hidetoshi, Hiramatsu, Kei, Yoshino, Toko, Kazuki, Kanako, Ishihara, Chie, Takehara, Shoko, Higaki, Katsumi, Nakagawa, Masato, Takahashi, Kazutoshi, Yamanaka, Shinya, Oshimura, Mitsuo
Formato: Texto
Lenguaje:English
Publicado: Nature Publishing Group 2009
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC2839293/
https://www.ncbi.nlm.nih.gov/pubmed/19997091
http://dx.doi.org/10.1038/mt.2009.274