The role of enzyme replacement therapy in severe Hunter syndrome—an expert panel consensus

Intravenous enzyme replacement therapy (ERT) with idursulfase for Hunter syndrome has not been demonstrated to and is not predicted to cross the blood–brain barrier. Nearly all published experience with ERT with idursulfase has therefore been in patients without cognitive impairment (attenuated phen...

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Detalles Bibliográficos
Autores principales: Muenzer, Joseph, Bodamer, Olaf, Burton, Barbara, Clarke, Lorne, Frenking, Gudrun Schulze, Giugliani, Roberto, Jones, Simon, Rojas, Maria Verónica Muñoz, Scarpa, Maurizio, Beck, Michael, Harmatz, Paul
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer-Verlag 2011
Materias:
Original Paper
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3249184/
https://www.ncbi.nlm.nih.gov/pubmed/22037758
http://dx.doi.org/10.1007/s00431-011-1606-3

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3249184/
https://www.ncbi.nlm.nih.gov/pubmed/22037758
http://dx.doi.org/10.1007/s00431-011-1606-3

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