Multicomponent nanoparticles as nonviral vectors for the treatment of Fabry disease by gene therapy

PURPOSE: Gene-mediated enzyme replacement is a reasonable and highly promising approach for the treatment of Fabry disease (FD). The objective of the present study was to demonstrate the potential applications of solid lipid nanoparticle (SLN)-based nonviral vectors for the treatment of FD. METHODS:...

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Detalles Bibliográficos
Autores principales: Ruiz de Garibay, Aritz Pérez, Delgado, Diego, del Pozo-Rodríguez, Ana, Solinís, María Ángeles, Gascón, Alicia Rodríguez
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Dove Medical Press 2012
Materias:
Original Research
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3484727/
https://www.ncbi.nlm.nih.gov/pubmed/23118528
http://dx.doi.org/10.2147/DDDT.S36131

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3484727/
https://www.ncbi.nlm.nih.gov/pubmed/23118528
http://dx.doi.org/10.2147/DDDT.S36131

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