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Multicomponent nanoparticles as nonviral vectors for the treatment of Fabry disease by gene therapy

PURPOSE: Gene-mediated enzyme replacement is a reasonable and highly promising approach for the treatment of Fabry disease (FD). The objective of the present study was to demonstrate the potential applications of solid lipid nanoparticle (SLN)-based nonviral vectors for the treatment of FD. METHODS:...

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Detalles Bibliográficos
Autores principales:	Ruiz de Garibay, Aritz Pérez, Delgado, Diego, del Pozo-Rodríguez, Ana, Solinís, María Ángeles, Gascón, Alicia Rodríguez
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Dove Medical Press 2012
Materias:	Original Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3484727/ https://www.ncbi.nlm.nih.gov/pubmed/23118528 http://dx.doi.org/10.2147/DDDT.S36131

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