Multiple exon skipping strategies to by-pass dystrophin mutations

Manipulation of dystrophin pre-mRNA processing offers the potential to overcome mutations in the dystrophin gene that would otherwise lead to Duchenne muscular dystrophy. Dystrophin mutations will require the removal of one or more exons to restore the reading frame and in some cases, multiple exon...

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Detalles Bibliográficos
Autores principales: Adkin, Carl F., Meloni, Penelope L., Fletcher, Susan, Adams, Abbie M., Muntoni, Francesco, Wong, Brenda, Wilton, Steve D.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Pergamon Press 2012
Materias:
Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3488593/
https://www.ncbi.nlm.nih.gov/pubmed/22182525
http://dx.doi.org/10.1016/j.nmd.2011.10.007

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3488593/
https://www.ncbi.nlm.nih.gov/pubmed/22182525
http://dx.doi.org/10.1016/j.nmd.2011.10.007

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