Evaluation of miglustat as maintenance therapy after enzyme therapy in adults with stable type 1 Gaucher disease: a prospective, open-label non-inferiority study

BACKGROUND: Previous studies have provided equivocal data on the use of miglustat as maintenance therapy in Gaucher disease type 1. We report findings from a clinical trial evaluating the effects of miglustat treatment in patients with stable type 1 Gaucher disease after enzyme therapy. METHODS: Adu...

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Detalles Bibliográficos
Autores principales: Cox, Timothy M, Amato, Dominick, Hollak, Carla EM, Luzy, Cecile, Silkey, Mariabeth, Giorgino, Ruben, Steiner, Robert D
Formato: Online Artículo Texto
Lenguaje:English
Publicado: BioMed Central 2012
Materias:
Research
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3552937/
https://www.ncbi.nlm.nih.gov/pubmed/23270487
http://dx.doi.org/10.1186/1750-1172-7-102

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3552937/
https://www.ncbi.nlm.nih.gov/pubmed/23270487
http://dx.doi.org/10.1186/1750-1172-7-102

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