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Enzyme replacement therapy for Fabry disease: A systematic review and meta-analysis

The specific treatment available for Fabry disease (FD) is enzyme replacement therapy (ERT) with agalsidase alfa or beta. A systematic review and meta-analysis was conducted to assess the efficacy and safety of ERT for FD. Only double-blind, randomized clinical trials (RCTs) comparing agalsidase alf...

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Detalles Bibliográficos
Autores principales: Alegra, Taciane, Vairo, Filippo, de Souza, Monica V., Krug, Bárbara C., Schwartz, Ida V.D.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Sociedade Brasileira de Genética 2012
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3571424/
https://www.ncbi.nlm.nih.gov/pubmed/23413206