THE 6-MINUTE WALK TEST AND OTHER ENDPOINTS IN DUCHENNE MUSCULAR DYSTROPHY: LONGITUDINAL NATURAL HISTORY OBSERVATIONS OVER 48 WEEKS FROM A MULTICENTER STUDY

Introduction: Duchenne muscular dystrophy (DMD) subjects ≥5 years with nonsense mutations were followed for 48 weeks in a multicenter, randomized, double-blind, placebo-controlled trial of ataluren. Placebo arm data (N = 57) provided insight into the natural history of the 6-minute walk test (6MWT)...

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Detalles Bibliográficos
Autores principales: Mcdonald, Craig M, Henricson, Erik K, Abresch, R Ted, Florence, Julaine M, Eagle, Michelle, Gappmaier, Eduard, Glanzman, Allan M, Spiegel, Robert, Barth, Jay, Elfring, Gary, Reha, Allen, Peltz, Stuart
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Blackwell Publishing Ltd 2013
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Main Articles
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3824082/
https://www.ncbi.nlm.nih.gov/pubmed/23681930
http://dx.doi.org/10.1002/mus.23902

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3824082/
https://www.ncbi.nlm.nih.gov/pubmed/23681930
http://dx.doi.org/10.1002/mus.23902

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