In vitro and In vivo Model Systems for Hemophilia A Gene Therapy

Hemophilia A is a hereditary disorder caused by various mutations in factor VIII gene resulting in either a severe deficit or total lack of the corresponding activity. Recent success in gene therapy of a related disease, hemophilia B, gives new hope that similar success can be achieved for hemophili...

Descripción completa

Detalles Bibliográficos
Autores principales: Mao, Jianhua, Xi, Xiaodong, Kapranov, Philipp, Dong, Biao, Firrman, Jenni, Xu, Ruian, Xiao, Weidong
Formato: Online Artículo Texto
Lenguaje:English
Publicado: 2013
Materias:
Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4229687/
https://www.ncbi.nlm.nih.gov/pubmed/25401041
http://dx.doi.org/10.4172/2157-7412.S1-014

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4229687/
https://www.ncbi.nlm.nih.gov/pubmed/25401041
http://dx.doi.org/10.4172/2157-7412.S1-014

Ejemplares similares