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In vitro and In vivo Model Systems for Hemophilia A Gene Therapy
Hemophilia A is a hereditary disorder caused by various mutations in factor VIII gene resulting in either a severe deficit or total lack of the corresponding activity. Recent success in gene therapy of a related disease, hemophilia B, gives new hope that similar success can be achieved for hemophili...
| Autores principales: | , , , , , , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
| Publicado: |
2013
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| Materias: | |
| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4229687/ https://www.ncbi.nlm.nih.gov/pubmed/25401041 http://dx.doi.org/10.4172/2157-7412.S1-014 |