Spinal Muscular Atrophy Therapeutics: Where do we Stand?

Spinal muscular atrophy (SMA) is an inherited neuromuscular disorder pathologically characterized by the degeneration of motor neurons in the spinal cord and muscle atrophy. Motor neuron loss often results in severe muscle weakness causing affected infants to die before reaching 2 years of age. Pati...

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Detalles Bibliográficos
Autores principales: d’Ydewalle, Constantin, Sumner, Charlotte J.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer US 2015
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4404440/
https://www.ncbi.nlm.nih.gov/pubmed/25631888
http://dx.doi.org/10.1007/s13311-015-0337-y

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4404440/
https://www.ncbi.nlm.nih.gov/pubmed/25631888
http://dx.doi.org/10.1007/s13311-015-0337-y

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