B-cell reconstitution after lentiviral vector–mediated gene therapy in patients with Wiskott-Aldrich syndrome

BACKGROUND: Wiskott-Aldrich syndrome (WAS) is a severe X-linked immunodeficiency characterized by microthrombocytopenia, eczema, recurrent infections, and susceptibility to autoimmunity and lymphomas. Hematopoietic stem cell transplantation is the treatment of choice; however, administration of WAS...

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Detalles Bibliográficos
Autores principales: Castiello, Maria Carmina, Scaramuzza, Samantha, Pala, Francesca, Ferrua, Francesca, Uva, Paolo, Brigida, Immacolata, Sereni, Lucia, van der Burg, Mirjam, Ottaviano, Giorgio, Albert, Michael H., Grazia Roncarolo, Maria, Naldini, Luigi, Aiuti, Alessandro, Villa, Anna, Bosticardo, Marita
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Mosby 2015
Materias:
Immune Deficiencies, Infection, and Systemic Immune Disorders
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4559137/
https://www.ncbi.nlm.nih.gov/pubmed/25792466
http://dx.doi.org/10.1016/j.jaci.2015.01.035

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4559137/
https://www.ncbi.nlm.nih.gov/pubmed/25792466
http://dx.doi.org/10.1016/j.jaci.2015.01.035

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