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Intra‐arterial transplantation of HLA‐matched donor mesoangioblasts in Duchenne muscular dystrophy

Intra‐arterial transplantation of mesoangioblasts proved safe and partially efficacious in preclinical models of muscular dystrophy. We now report the first‐in‐human, exploratory, non‐randomized open‐label phase I–IIa clinical trial of intra‐arterial HLA‐matched donor cell transplantation in 5 Duche...

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Detalles Bibliográficos
Autores principales: Cossu, Giulio, Previtali, Stefano C, Napolitano, Sara, Cicalese, Maria Pia, Tedesco, Francesco Saverio, Nicastro, Francesca, Noviello, Maddalena, Roostalu, Urmas, Natali Sora, Maria Grazia, Scarlato, Marina, De Pellegrin, Maurizio, Godi, Claudia, Giuliani, Serena, Ciotti, Francesca, Tonlorenzi, Rossana, Lorenzetti, Isabella, Rivellini, Cristina, Benedetti, Sara, Gatti, Roberto, Marktel, Sarah, Mazzi, Benedetta, Tettamanti, Andrea, Ragazzi, Martina, Imro, Maria Adele, Marano, Giuseppina, Ambrosi, Alessandro, Fiori, Rossana, Sormani, Maria Pia, Bonini, Chiara, Venturini, Massimo, Politi, Letterio S, Torrente, Yvan, Ciceri, Fabio
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2015
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4693504/
https://www.ncbi.nlm.nih.gov/pubmed/26543057
http://dx.doi.org/10.15252/emmm.201505636