Effect of ivacaftor treatment in patients with cystic fibrosis and the G551D-CFTR mutation: patient-reported outcomes in the STRIVE randomized, controlled trial

BACKGROUND: Cystic fibrosis (CF) is an inherited, rare autosomal recessive disease that results in chronically debilitating morbidities and high premature mortality. We evaluated how ivacaftor treatment affected CF symptoms, functioning, and well-being, as measured by the Cystic Fibrosis Questionnai...

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Detalles Bibliográficos
Autores principales: Quittner, Alexandra, Suthoff, Ellison, Rendas-Baum, Regina, Bayliss, Martha S., Sermet-Gaudelus, Isabelle, Castiglione, Brenda, Vera-Llonch, Montserrat
Formato: Online Artículo Texto
Lenguaje:English
Publicado: BioMed Central 2015
Materias:
Research
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4702321/
https://www.ncbi.nlm.nih.gov/pubmed/26135562
http://dx.doi.org/10.1186/s12955-015-0293-6

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4702321/
https://www.ncbi.nlm.nih.gov/pubmed/26135562
http://dx.doi.org/10.1186/s12955-015-0293-6

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