Patterns of disease progression in type 2 and 3 SMA: Implications for clinical trials

The aim of the study was to establish 12-month changes in the Hammersmith Functional motor scale in a large cohort of SMA patients, to identify patterns of disease progression and the effect of different variables. 268 patients were included in this multicentric study. Their age ranged between 2.5 a...

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Detalles Bibliográficos
Autores principales: Mercuri, Eugenio, Finkel, Richard, Montes, Jacqueline, Mazzone, Elena S., Sormani, Maria Pia, Main, Marion, Ramsey, Danielle, Mayhew, Anna, Glanzman, Allan M., Dunaway, Sally, Salazar, Rachel, Pasternak, Amy, Quigley, Janet, Pane, Marika, Pera, Maria Carmela, Scoto, Mariacristina, Messina, Sonia, Sframeli, Maria, Vita, Gian Luca, D'Amico, Adele, van den Hauwe, Marleen, Sivo, Serena, Goemans, Nathalie, Kaufmann, Petra, Darras, Basil T., Bertini, Enrico, Muntoni, Francesco, De Vivo, Darryl C.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Pergamon Press 2016
Materias:
Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4762230/
https://www.ncbi.nlm.nih.gov/pubmed/26776503
http://dx.doi.org/10.1016/j.nmd.2015.10.006

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4762230/
https://www.ncbi.nlm.nih.gov/pubmed/26776503
http://dx.doi.org/10.1016/j.nmd.2015.10.006

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