Genome-editing technologies for gene correction of hemophilia

Hemophilia is caused by various mutations in blood coagulation factor genes, including factor VIII (FVIII) and factor IX (FIX), that encode key proteins in the blood clotting pathway. Although the addition of therapeutic genes or infusion of clotting factors may be used to remedy hemophilia’s sympto...

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Detalles Bibliográficos
Autores principales: Park, Chul-Yong, Lee, Dongjin R., Sung, Jin Jea, Kim, Dong-Wook
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer Berlin Heidelberg 2016
Materias:
Perspective
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4999461/
https://www.ncbi.nlm.nih.gov/pubmed/27357631
http://dx.doi.org/10.1007/s00439-016-1699-x

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4999461/
https://www.ncbi.nlm.nih.gov/pubmed/27357631
http://dx.doi.org/10.1007/s00439-016-1699-x

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