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Genetic manipulation for inherited neurodegenerative diseases: myth or reality?
Rare genetic diseases affect about 7% of the general population and over 7000 distinct clinical syndromes have been described with the majority being due to single gene defects. This review will provide a critical overview of genetic strategies that are being pioneered to halt or reverse disease pro...
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
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BMJ Publishing Group
2016
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| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5050284/ https://www.ncbi.nlm.nih.gov/pubmed/27002113 http://dx.doi.org/10.1136/bjophthalmol-2015-308329 |