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Treosulfan-Based Conditioning Regimen in Sibling and Alternative Donor Hematopoietic Stem Cell Transplantation for Children with Sickle Cell Disease

BACKGROUND AND OBJECTIVES: Lack of suitable donors and regimen related toxicity are major barriers for hematopoietic stem cell transplantation (HSCT) in patients with sickle cell disease (SCD). The aim of the study is the assessment of efficacy and toxicity of Treosulfan-based conditioning regimen f...

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Detalles Bibliográficos
Autores principales: Marzollo, Antonio, Calore, Elisabetta, Tumino, Manuela, Pillon, Marta, Gazzola, Maria Vittoria, Destro, Roberta, Colombatti, Raffaella, Marson, Piero, Tison, Tiziana, Colpo, Anna, Mainardi, Chiara, Gabelli, Maria, Boaro, Maria Paola, Rossin, Sara, Strano, Aurora, Quaglia, Nadia, Menzato, Federica, Basso, Giuseppe, Sainati, Laura, Messina, Chiara
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Università Cattolica del Sacro Cuore 2017
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5333731/
https://www.ncbi.nlm.nih.gov/pubmed/28293402
http://dx.doi.org/10.4084/MJHID.2017.014