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Letter to the Editors: Concerning “Divergent clinical outcomes of alphaglucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi M et al.

Detalles Bibliográficos
Autores principales: Ortolano, Rita, Baronio, Federico, Masetti, Riccardo, Prete, Arcangelo, Cassio, Alessandra, Pession, Andrea
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Elsevier 2017
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5344415/
https://www.ncbi.nlm.nih.gov/pubmed/28316933
http://dx.doi.org/10.1016/j.ymgmr.2017.02.003