Early intervention with tafamidis provides long-term (5.5-year) delay of neurologic progression in transthyretin hereditary amyloid polyneuropathy

Transthyretin hereditary amyloid polyneuropathy, also traditionally known as transthyretin familial amyloid polyneuropathy (ATTR-FAP), is a rare, relentless, fatal hereditary disorder. Tafamidis, an oral, non-NSAID, highly specific transthyretin stabilizer, demonstrated safety and efficacy in slowin...

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Detalles Bibliográficos
Autores principales: Waddington Cruz, Márcia, Amass, Leslie, Keohane, Denis, Schwartz, Jeffrey, Li, Huihua, Gundapaneni, Balarama
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Taylor & Francis 2016
Materias:
Original Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5359776/
https://www.ncbi.nlm.nih.gov/pubmed/27494299
http://dx.doi.org/10.1080/13506129.2016.1207163

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5359776/
https://www.ncbi.nlm.nih.gov/pubmed/27494299
http://dx.doi.org/10.1080/13506129.2016.1207163

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