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Retinal Gene Therapy: Surgical Vector Delivery in the Translation to Clinical Trials

An exceptionally high number of monogenic disorders lead to incurable blindness, making them targets for the development of gene-therapy. In order to successfully apply therapeutic vector systems in vivo, the heterogeneity of the disease phenotype needs to be considered. This necessitates tailored a...

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Detalles Bibliográficos
Autores principales: Ochakovski, G. Alex, Bartz-Schmidt, K. Ulrich, Fischer, M. Dominik
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Frontiers Media S.A. 2017
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5376580/
https://www.ncbi.nlm.nih.gov/pubmed/28420956
http://dx.doi.org/10.3389/fnins.2017.00174