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Retinal Gene Therapy: Surgical Vector Delivery in the Translation to Clinical Trials
An exceptionally high number of monogenic disorders lead to incurable blindness, making them targets for the development of gene-therapy. In order to successfully apply therapeutic vector systems in vivo, the heterogeneity of the disease phenotype needs to be considered. This necessitates tailored a...
| Autores principales: | , , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
| Publicado: |
Frontiers Media S.A.
2017
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| Materias: | |
| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5376580/ https://www.ncbi.nlm.nih.gov/pubmed/28420956 http://dx.doi.org/10.3389/fnins.2017.00174 |