Enhancement of β‐Globin Gene Expression in Thalassemic IVS2‐654 Induced Pluripotent Stem Cell‐Derived Erythroid Cells by Modified U7 snRNA

The therapeutic use of patient‐specific induced pluripotent stem cells (iPSCs) is emerging as a potential treatment of β‐thalassemia. Ideally, patient‐specific iPSCs would be genetically corrected by various approaches to treat β‐thalassemia including lentiviral gene transfer, lentivirus‐delivered s...

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Detalles Bibliográficos
Autores principales: Phanthong, Phetcharat, Borwornpinyo, Suparerk, Kitiyanant, Narisorn, Jearawiriyapaisarn, Natee, Nuntakarn, Lalana, Saetan, Jirawat, Nualkaew, Tiwaporn, Sa‐ngiamsuntorn, Khanit, Anurathapan, Usanarat, Dinnyes, Andras, Kitiyanant, Yindee, Hongeng, Suradej
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2017
Materias:
Translational Research Articles and Reviews
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5442829/
https://www.ncbi.nlm.nih.gov/pubmed/28213976
http://dx.doi.org/10.1002/sctm.16-0121

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5442829/
https://www.ncbi.nlm.nih.gov/pubmed/28213976
http://dx.doi.org/10.1002/sctm.16-0121

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